Kiss, Ace Frehley and Gene Simmons
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A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two years after the treatment.
Eli Lilly said on Friday it would acquire gene therapy developer Adverum Biotechnologies in a deal valued at up to $261.7 million, aiming to strengthen its pipeline with an experimental eye disease treatment.
Scientists have identified mutations in the CPD gene as a key cause of a rare congenital hearing loss, revealing how disruptions in arginine and nitric oxide signaling damage sensory cells in the ear.
The arrival of agriculture coincided with a sharp rise in a gene variant that protected against the virus that causes winter vomiting, researchers from Karolinska Institutet and Linköping University report after analyzing DNA from over 4,
The researchers used Crispr-Cas9 “genetic scissors” technology to make the edit in pig zygotes — the cells formed from the fertilisation of eggs with sperm. These were then implanted into a surrogate female pig, who gave birth to the genetically engineered piglets.
The actor, who died this year at 95, led a quiet life in New Mexico. An auction of his belongings offers insights into his life and work.
Some genetic disorders—such as cystic fibrosis, hemophilia and Tay Sachs disease—involve many mutations in a person's genome, often with enough variation that even two individuals who share the same disorder might have a different combination of mutations.
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