News

Columnist Shalom Lim will continue to pursue the themes that matter to him as a person with Duchenne MD, but as a writer now, ...
Preliminary data are expected this year for a Phase 1/2 clinical trial testing the investigational therapy SRP-1003 in DM1.
Preliminary data are expected this year for a Phase 1/2 clinical trial testing the investigational therapy SRP-1003 in DM1.
Agamree, an approved steroid treatment for Duchenne MD, will be sold in Turkey by GEN, per an agreement with Santhera.
Columnist Robin Stemple, his brothers, and more enjoy a long-in-the works family music celebration at his mother's nursing home.
A protein called MYOD has long been known to be able to turn on genes, but a recent study has found that it also can turn off ...
In both good times and bad, the importance of human connection cannot be understated, columnist Patrick Moeschen writes.
Enrollment is now ongoing in a first-in-human clinical trial testing EPI-321, a therapy designed to target the underlying ...
Columnist Shalom Lin and his partner, Amanda — both disabled artists — find that their challenges are exactly what can drive ...
The FDA has granted breakthrough therapy designation to DYNE-251 for the treatment of DMD in patients amenable to exon 51 skipping.
Columnist Robin Stemple treasured the time with his family during a recent weekend trip, but fears his FSHD will soon make travel impossible.