News

Columnist Shalom Lim will continue to pursue the themes that matter to him as a person with Duchenne MD, but as a writer now, ...
Preliminary data are expected this year for a Phase 1/2 clinical trial testing the investigational therapy SRP-1003 in DM1.
Agamree, an approved steroid treatment for Duchenne MD, will be sold in Turkey by GEN, per an agreement with Santhera.